Defining a new era of oligonucleotides

Defining a new era of oligonucleotides

We are a biotechnology company focused on delivering transformational therapies for patients with serious, genetically-defined diseases.

Our chemistry platform enables the creation of highly specific, well characterized oligonucleotides designed to deliver superior efficacy and safety across multiple therapeutic modalities. Our pipeline is initially focused on neurological disorders and extends across several other therapeutic areas.

1 st

first to design and bring stereopure and
allele-specific medicines to clinic


clinical studies initiated in 2017


nucleic acid modalities being advanced with Wave stereopure chemistry


discovery programs


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